ASGCT News

Read the ASGCT-Citeline 2025 Q2 Landscape Analysis Field Report

Read + download the report | August 01, 2025

In Q2, three new therapeutics were approved and the number of gene therapy programs continued to climb.

Publications

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Behind the Breakthroughs: What Every Caregiver Should Know About Clinical Trial Design

Ali Kujawski, MPH, Senior Patient Outreach Manager | July 23, 2025

For families facing rare diseases, clinical trials often represent more than just a research protocol—they represent hope. But what actually goes into designing those trials?

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A Vaccine for Cocaine Addiction with Dr. Stephen Kaminsky

Listen + subscribe | July 22, 2025

During the 2025 Annual Meeting, Dr. Kaminsky presented results from a phase 1 clinical trial describing a vaccine for cocaine addiction.

Annual Meeting 2025  |  Podcasts

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Gene and Cell Therapy in Africa: Reflections on My ASGCT Journey

Irene Honam Tsey, PhD | July 16, 2025

Irene Honam Tsey, a research fellow at the University of Health and Allied Sciences (UHAS) in Ghana, attended the 2025 ASGCT Annual Meeting in New Orleans in May.

Annual Meeting 2025

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25 Years of Molecular Therapy with Drs. Beverly Davidson and Jeff Chamberlain

Listen + subscribe to the ASGCT Podcast Network | July 16, 2025

Listen to this episode of the Molecular Therapy Podcast on the ASGCT Podcast Network!

Podcasts

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Takeaways from the 7th Annual FDA Liaison Meeting

Andrew Liermann | July 15, 2025

The meeting featured two ASGCT-led presentations addressing challenges and opportunities in regulatory policy for CGT development.

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Developing Therapeutic Platforms with Dr. P.J. Brooks

Listen + subscribe to the ASGCT Podcast Network | July 09, 2025

"I think what we're really seeing as a therapeutic platform emerging is particularly genome editing with the idea that...we're looking at an editor and a delivery system and applying that to more than one disease."

Annual Meeting 2025  |  Podcasts

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Navigating Funding and Development Challenges for Transformative Therapies

Caitlin McCombs, MBA | July 09, 2025

CGT development stands at a critical juncture as the field addresses unique challenges distinct from traditional pharmaceutical development pathways.

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Lessons from the Frontlines of CGT Trials

Lexi Starosta | July 08, 2025

“The assumption is that we’ll do anything to save our child...But we also know how to say no when the risk doesn’t match the reward.”

Outreach

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Regulatory Innovation Paves the Way for Faster Access to Life-Saving Cell and Gene Therapies

Andrew Liermann  | June 23, 2025

From FDA's START Pilot Program to global harmonization efforts, these innovations collectively address barriers to development and accelerate patient access to transformative therapies. 

Annual Meeting 2025

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The Ups and Downs of Conducting Groundbreaking Research with Dr. Kiran Musunuru

Listen + subscribe to the ASGCT Podcast Network! | June 16, 2025

One day after presenting research that led to a first-of-its-kind medical breakthrough, Dr. Musunuru told us that there was so much more to the story.

Podcasts

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FDA Cell & Gene Therapy Roundtable: Putting Every Patient Within Reach of Innovation

Terry Flotte, MD, and Paula Cannon, PhD | June 11, 2025

Roughly 15 million Americans - about half of them children - live with rare genetic disorders, yet more than 100 clinical stage gene therapy programs have been shelved since early 2023.

Policy & Advocacy

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25 Years of Molecular Therapy with Sheila Mikhail and Dr. Mark Kay

Listen + subscribe to the ASGCT Podcast Network! | June 11, 2025

In this episode, Dr. Glorioso discusses two recent reviews published in Molecular Therapy with Sheila Mikhail and Dr. Mark Kay.

Molecular Therapy  |  Podcasts

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ASGCT Builds Bridges: Advancing Access Through Patient-Centered and Global Initiatives

Caitlin McCombs, MBA; Ali Kujawski, MPH; and Lexi Starosta | June 10, 2025

During #ASGCT2025, ASGCT reinforced its commitment to patient-centered approaches through multiple sessions designed to elevate patient voices and address access challenges for cell and gene therapies (CGTs). 

Annual Meeting 2025  |  Outreach  |  Policy & Advocacy

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ASGCT Congressional Briefing Highlights Transformative Potential of Gene Editing Technologies

Paula Cannon, PhD | June 10, 2025

Gene editing represents a paradigm shift in medicine, offering the possibility to address the root genetic causes of disease rather than just treating symptoms.

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From Trials to Triumph: Patient Advocates Share the Path from Research to Approval

Alison Kujawski, MPH | June 09, 2025

Check out our summary of a standout session during ASGCT's Empowering Patients Summit, The Journey from Early-stage Trials to Approval.

Outreach

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