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Stay Current with the Annual Meeting App

ASGCT Staff | February 11, 2020

The ASGCT 23rd Annual Meeting preliminary schedule is now available on the free meeting app.

 

Annual Meeting
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Sean Doerr Shares How He's Embracing Life with Pompe Disease

ASGCT Staff | February 06, 2020

In this Q&A, Sean Doerr, 29, talks about living his life with a genetic disorder that took years to diagnose, the importance of being your own advocate, and why he believes it's an "exciting time to have Pompe disease."

Patient Perspectives
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ASGCT Applauds FDA's Gene Therapy Guidance Documents

Adora Ndu, PharmD, J.D. | February 03, 2020

Dr. Ndu is chair of the ASGCT Regulatory Affairs Committee and Vice President of Regulatory Affairs; Policy, Research, Engagement (PRE) & International at BioMarin Pharmaceutical Inc.

Policy Updates
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Abstracts Deadline Extended for the 23rd Annual Meeting

ASGCT Staff | January 29, 2020

There's still time to seize the opportunity to present your work to more than 5,000 leaders in the field of gene and cell therapy.

Annual Meeting
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Advocacy Reflects on Accomplishments and Looks Ahead to Future Efforts

ASGCT Staff | January 20, 2020

Learn about ASGCT's advocacy accomplishments in 2019 and our priorities for 2020.

Advocacy
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ASGCT Releases Three-Year Strategic Plan

Edith Pfister, Ph.D. | January 16, 2020

Gene and cell therapies are rapidly transforming medicine. Read the full 2020 strategic plan to understand where ASGCT is heading, and why.

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Watch "Life After Gene Therapy" from ASGCT and NORD

ASGCT Staff | January 10, 2020

The fifth and final webinar in this series explores the personal journeys  of two patients who received gene therapy.

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ASGCT Invited to Join USP as a Voting Member

ASGCT Staff | January 08, 2020

ASGCT’s Regulatory Affairs Committee Chair, Adora Ndu, PharmD, J.D., (pictured below at the Policy Summit) will serve as the ASGCT delegate to the USP Convention for a five-year cycle.

Policy Updates
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Policy Summit Slides Are Now Available

ASGCT Staff | December 18, 2019

We're excited to offer presentation slides to all of our members from the 2019 ASGCT Policy Summit last month in Washington, D.C.

Policy Summit
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Make a Virtual Visit to the 2019 Annual Meeting

ASGCT Staff | December 17, 2019

Videos from the ASGCT 22nd Annual Meeting are now available on our YouTube channel.

Annual Meeting
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ASGCT Holds Second Annual FDA Liaison Meeting

ASGCT Staff | December 11, 2019

ASGCT members presented on three topics to staff of the Office of Tissues and Advanced Therapies (OTAT), providing ASGCT recommendations to the Agency on regulatory topics of mutual interest in the field. Below, Wilson Bryan, MD, director of the FDA OTAT, acknowledges his staff during the discussion about common gene therapy IND deficiences and recommendations for improvement.

Advocacy
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Watch “Understanding the Gene Therapy Process and Aftercare,” from ASGCT and NORD

ASGCT Staff | December 06, 2019

The webinars in this series are designed to inform patients, patient advocates, families, and the public about various aspects of gene therapy.

Education
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Learn About Blood Cancers and CAR T-Cell Therapy

ASGCT Staff | December 03, 2019

CAR T-cell therapy is a treatment approach that helps the immune system recognize cancer cells as a threat and eliminate them.

Education
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Register Today for ASGCT's 23rd Annual Meeting in Boston

ASGCT Staff | December 02, 2019

The annual meeting, which will be held May 12-15, 2020 in Boston, will return to a convention center for the first time in seven years.

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(From left) Michael C. Burgess, MD (R-TX) (with Matthew Porteus, M.D., Ph.D., and Jennelle Stephenson), and Danny K. Davis (D-IL), gave remarks emphasizing the importance of supporting sickle cell disease research.

ASGCT Co-Hosts Second Congressional Briefing on Sickle Cell Disease

ASGCT Staff | November 26, 2019

ASGCT co-hosted a briefing on Capitol Hill to hightlight how policymakers can support sickle cell disease (SCD) screening as well as treatment development and access.

Advocacy
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Meet the Editor: Gerhard Bauer, Molecular Therapy—Methods & Clinical Development

ASGCT Staff | November 25, 2019

ASGCT member and director of the Good Manufacturing Practice (GMP) laboratory at the UC Davis Institute for Regenerative Cures Gerhard Bauer will become the editor-in-chief of ASGCT's journal, Molecular Therapy—Methods & Clinical Development on January 1, 2020.

Molecular Therapy
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2020

23rd Annual Meeting

May 12-15 | Boston