Excellence in Research Award


About the Award

Each year the ASGCT Abstract Review Committee for the Annual Meeting selects the top six abstracts submitted by students and fellows to receive Excellence in Research Awards. Recipients of the Excellence in Research Awards are announced at the end of the George Stamatoyannopoulos plenary lecture on Thursday, May 17, 2018 and will receive a monetary award of $500 along with a special plaque.

Criteria and Selection

Any ASGCT Member or Associate Member who submits an abstract to the 2018 Annual Meeting is eligible to receive the award.  For more information, review the abstract submission guidelines coming soon.

Recipients

2016 
Angelo Amabile, San Raffaele Telethon Institute for Gene Therapy
Inheritable Silencing of Endogenous Gene by Hit-and-Run Targeted Epigenetic Editing

Maria Carmina Castiello, San Raffaele Telethon Institute for Gene Therapy
Lentiviral-Mediated Gene Therapy Restores B Cell Homeostasis and Tolerance in Wiskott-Aldrich Syndrome Patients

Mei Dai, Cincinnati Children’s Hospital Medical Center
Platelets Transfusion New Role as Brain Therapeutics for Acute Neuronopathic Gaucher Disease

Adele Mucci, Hannover Medical School
Murine iPSC-Derived Macrophages Improve the In Vivo Disease Phenotype of Pulmonary Alveolar Proteinosis Due to Csf2rb Deficiency

Christopher Nelson, Duke University
Local and Systemic Gene Editing in a Mouse Model of Duchenne Muscular Dystrophy

Mohammadsharif Tabebordbar, Harvard University
In Vivo DMD Gene Editing in Muscles and Muscle Stem Cells of Dystrophic Mice

2015 
Garrett Berry, University of North Carolina-Chapel Hill
Pharmacological Regulation of Vesicular Trafficking as a Strategy to Enhance Recombinant AAV Transduction

Mari Hirvinen, University of Helsinki
Boosting the Immunogenicity of an Oncolytic Vaccinia Virus By Expression of DAI Can Enhance Anti-Tumor Immunity in Humanized Mice

Ulrike Jung, Beckman Research Institute of City of Hope
A Novel RNAi Trigger Design Retains Potent, Target Specific Activity Despite Emerging Mutations in the Target Site

Shruthi Naik, Mayo Clinic
Safety, Toxicity and Efficacy of Systemic Recombinant VSV Therapy in Pet Dogs With Spontaneous Cancer

Lauren Toth, Duke University
A Light-Inducible CRISPR/Cas9 System for Control of Endogenous Gene Activation

Erika Zonari, San Raffaele Telethon Institute for Gene Therapy (TIGET)
Hematopoietic Stem Cell Gene Therapy (2.0) Based on Purified CD34+CD38- Cells

2014 
Swaroopa Guda, Boston Childrens Hospital
Optimization of Lentivirus Vector RNA Polymerase II Driven microRNA Embedded shRNAs for Enhanced Processing and Efficient Knockdown of Bcl11a for Induction of Fetal Hemoglobin in Erythroid Cells

Juliette Hordeaux, University of Nantes
Long-term Neurologic Correction in the Pompe Disease Mice by Intrathecal Gene Therapy

Sharon Lam, Baylor College of Medicine
Ex Vivo Expanded Multi-Specific Cytotoxic T Lymphocytes Derived from HIV+ Patients and HIV Negative Donors Using GMP Compliant Methodologies Suppress HIV Replication

Michelle Marcus, Northwestern Univeristy
Engineering Exosomes as Therapeutic Delivery Vehicles

Nobuhiro Nishio, Nagoya University Hospital
Combined Armed Oncolytic Virus and CAR-T Cells Counter the Hostile Environment of Solid Tumors

Lukasz Swiech, Broad Institute
CRISPR-Mediated Genome Editing in the Mammalian Brain

2013 
Luca Biasco, San Raffaele Telethon Institute for Gene Therapy
Comprehensive Study of Lentiviral [quot]Integrome[quot] in WAS Gene Therapy Patients

Sourav Choudhury, University of Massachusetts Medical School
Identification of Novel Vectors Capable of CNS Transduction in Adult Mice after Single Round Selection Using DNA Shuffled AAV Capsid Library

Drew Deniger, University of Texas MD Anderson Cancer Center
Clinical Implications of ROR1-Specific T Cells That Target B-Cell Leukemia

Charles Lai, Massachusetts General Hospital
Non-Invasive In Vivo Imaging, Biodistribution and Clearance Analyses of Intravenously Administered Extracellular Vesicles

Rajiv Sharma, Children's Hospital of Philadelphia
In Vivo ZFN Mediated Targeting of Albumin as a Platform for Expression of Multiple Therapeutic Genes

Barbara Smith, University of Florida
Acid alpha-Glucosidase Gene Replacement Therapy to the Diaphragm in Ventilator-Dependent Pompe Disease: One-Year Respiratory Motor Outcomes

2012 
Anthony S. Fargnoli, University of Pennsylvania
Molecular Cardiac Surgery Mediated ssAAV1-SERCA2a Gene Therapy Restores Global and Regional Contractility in Ovine Ischemic Cardiomyopathy

Alice Giustacchini, San Raffaele Telethon Institute for Gene Therapy
microRNA 126 Is a New Regulator of Hematopoietic Stem Cells Homeostasis

Patrick J. Hanley, Baylor College of Medicine
Phase I Study To Improve Virus-Specific Immune Reconstitution after Cord Blood Transplantation Using Cord Blood-Derived Virus-Specific T Cells

Nicholas W. Keiser, University of Iowa
CFTR Gene Correction of Only the Surface Airway Epithelium Restores Antimicrobial Activity to CFTR Knockout Ferret Tracheas Ex Vivo

Rajiv Sharma, Children's Hospital of Philadelphia
Correction of Hemophilia B Phenotype Following ZFN Mediated Genome Editing in Adult Mice

Korashon L. Watts, Fred Hutchinson Cancer Research Center
Transfusion Independence and Rapid Engraftment of Nonhuman Primate Cord Blood Cells Expanded with the Combination of HOXB4 and Delta Ligand
 

2019
22nd Annual Meeting
April 29 – May 2 | Washington D.C.
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