ASGCT News

25 Years of Molecular Therapy with Drs. Rayne Rouce and Joseph Glorioso

Listen + subscribe wherever you get your podcasts! | August 08, 2025

Listen to this episode of the Molecular Therapy Podcast on the ASGCT Podcast Network!

Molecular Therapy  |  Podcasts

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Access to a Cure: Ensuring Equitable Access to Cell and Gene Therapies for Children with Sickle Cell Disease

ASGCT Partners with Children’s Hospital Association on Sickle Cell Disease Access

Christina Mayer | August 04, 2025

Achieving equitable access to gene therapies requires coordinated action across clinical care delivery, healthcare administration, and payment policy. By tackling the issues raised at the briefing, we can help ensure the next generation of SCD therapies reach patients, wherever they are.

Policy & Advocacy

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Building a Vision with Dr. Mimi Lee

Listen + subscribe on the ASGCT Podcast Network! | August 04, 2025

Listen to Dr. Mimi Lee talk about her vision to prevent and treat diseases for every unique individual at the genetic level.

Annual Meeting 2025  |  Podcasts

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Read the ASGCT-Citeline 2025 Q2 Landscape Analysis Field Report

Read + download the report | August 01, 2025

In Q2, three new therapeutics were approved and the number of gene therapy programs continued to climb.

Publications

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Behind the Breakthroughs: What Every Caregiver Should Know About Clinical Trial Design

Ali Kujawski, MPH, Senior Patient Outreach Manager | July 23, 2025

For families facing rare diseases, clinical trials often represent more than just a research protocol—they represent hope. But what actually goes into designing those trials?

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A Vaccine for Cocaine Addiction with Dr. Stephen Kaminsky

Listen + subscribe | July 22, 2025

During the 2025 Annual Meeting, Dr. Kaminsky presented results from a phase 1 clinical trial describing a vaccine for cocaine addiction.

Annual Meeting 2025  |  Podcasts

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Gene and Cell Therapy in Africa: Reflections on My ASGCT Journey

Irene Honam Tsey, PhD | July 16, 2025

Irene Honam Tsey, a research fellow at the University of Health and Allied Sciences (UHAS) in Ghana, attended the 2025 ASGCT Annual Meeting in New Orleans in May.

Annual Meeting 2025

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25 Years of Molecular Therapy with Drs. Beverly Davidson and Jeff Chamberlain

Listen + subscribe to the ASGCT Podcast Network | July 16, 2025

Listen to this episode of the Molecular Therapy Podcast on the ASGCT Podcast Network!

Podcasts

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Takeaways from the 7th Annual FDA Liaison Meeting

Andrew Liermann | July 15, 2025

The meeting featured two ASGCT-led presentations addressing challenges and opportunities in regulatory policy for CGT development.

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Developing Therapeutic Platforms with Dr. P.J. Brooks

Listen + subscribe to the ASGCT Podcast Network | July 09, 2025

"I think what we're really seeing as a therapeutic platform emerging is particularly genome editing with the idea that...we're looking at an editor and a delivery system and applying that to more than one disease."

Annual Meeting 2025  |  Podcasts

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Navigating Funding and Development Challenges for Transformative Therapies

Caitlin McCombs, MBA | July 09, 2025

CGT development stands at a critical juncture as the field addresses unique challenges distinct from traditional pharmaceutical development pathways.

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Lessons from the Frontlines of CGT Trials

Lexi Starosta | July 08, 2025

“The assumption is that we’ll do anything to save our child...But we also know how to say no when the risk doesn’t match the reward.”

Outreach

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Regulatory Innovation Paves the Way for Faster Access to Life-Saving Cell and Gene Therapies

Andrew Liermann  | June 23, 2025

From FDA's START Pilot Program to global harmonization efforts, these innovations collectively address barriers to development and accelerate patient access to transformative therapies. 

Annual Meeting 2025

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The Ups and Downs of Conducting Groundbreaking Research with Dr. Kiran Musunuru

Listen + subscribe to the ASGCT Podcast Network! | June 16, 2025

One day after presenting research that led to a first-of-its-kind medical breakthrough, Dr. Musunuru told us that there was so much more to the story.

Podcasts

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FDA Cell & Gene Therapy Roundtable: Putting Every Patient Within Reach of Innovation

Terry Flotte, MD, and Paula Cannon, PhD | June 11, 2025

Roughly 15 million Americans - about half of them children - live with rare genetic disorders, yet more than 100 clinical stage gene therapy programs have been shelved since early 2023.

Policy & Advocacy

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25 Years of Molecular Therapy with Sheila Mikhail and Dr. Mark Kay

Listen + subscribe to the ASGCT Podcast Network! | June 11, 2025

In this episode, Dr. Glorioso discusses two recent reviews published in Molecular Therapy with Sheila Mikhail and Dr. Mark Kay.

Molecular Therapy  |  Podcasts

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