ASGCT Releases Patient Education Resources on Batten Disease

ASGCT Staff - September 30, 2020

We're highlighting the latest resources on our new Patient Education site, this week focusing on Batten disease.

ASGCT is highlighting its new resources focusing on gene therapy for Batten disease, which are now available on the new Patient Education site.

Batten disease is the common name for a group of rare genetic disorders that affect the nervous system. Each form of Batten is linked to a specific faulty gene that leads to waste buildup in cells. Gene therapy may offer a one-time treatment to slow or ideally stop the progression of these disorders by delivering a working gene to target the cause of the disease.

This is the third group of resources from ASGCT's Patient Education Program. During this round, we're releasing new pages, videos, and infographics on the Patient Education site. In the coming weeks, we'll highlight:

  • Fabry disease
  • Patient Journey, a set of resources to help guide patients through the challenging journey from diagnosis to pursuing gene therapy treatment

Let us know what you think of the new site and collection of resources by sending feedback to ASGCT Patient Outreach Manager Ali Kujawski.

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