News Archives for Gene Therapy Approval

Recent News

ASGCT Celebrates FDA Approval of Voretigene Neparvovec (Luxturna) as Treatment for Inherited Retinal Disease
December 19, 2017
Gene Therapy Approval Luxturna

Groundbreaking gene therapy is the first AAV viral vector product to be approved for use in the United States.

First CAR T Cell Therapy for Adults Approved by FDA

With Wednesday’s FDA approval of axicabtagene ciloleucel (Yescarta®, Kite Pharma, Inc/Gilead), the administration has put into clinicians’ hands the first CAR T cell therapy for adult patients with relapsed or refractory large B-cell lymphoma.

FDA Approves First CAR T Cell Treatment for Acute Lymphoblastic Leukemia

“We are incredibly excited to see a CAR T-cell treatment come to patients in the United States,” Dr. Helen E. Heslop, ASGCT President and Director of the Center for Cell and Gene Therapy at Baylor College of Medicine, Texas Children’s Hospital and Houston Methodist Hospital says. “This remarkable approval is the beginning of what we see as a chance to transform the way in which we treat cancer.”

22nd Annual Meeting
April 29 – May 2 | Washington D.C.