Stephanie Cherqui, PhD

University of California, San Diego, Associate Professor

What is your current professional status?

Associate Professor

What is your work setting (i.e. academic institution, government organization (i.e. FDA, NIH, etc.), bio-industry/pharmaceutical company, etc.)?

Academic institution / University

What is your scientific area of research?

Ex vivo hematopoietic stem cell gene therapy for multi-organ degenerative disorders

Why do you want to be a mentor?

I had really good mentors who helped me taking decisions during my career. Thus, I like to contribute advising young scientists and help them if possible.

As a mentor, what are you hoping to gain from this experience?

I like networking and meeting people, and I think it is interesting and important to learn what the new generation of scientists is facing. I am also researching young talented and motivated people to recruit in my lab.

How important are the following in the selection of a mentee: (1 – 5 scale, 1 = most important, 5 = least important)

  • Compatibility of Scientific Specialties: 3
  • Geographic Location: 4
  • Professional Status / Success: 3
  • Compatibility of Career Path: 1 (most)
  • Communication Style: 3

Summarize in a brief paragraph (150 words or less), please provide a biography that describes who you are and what you do in the field of gene and/or cell therapy:

The focus of my lab is to develop stem cell and gene therapy strategies for degenerative multi-systemic disorders, and to understand the mechanisms by which hematopoietic stem and progenitor cells (HSPC) can lead to tissue repair. My group's work is leading to the first-in-human clinical trial for autologous hematopoietic stem cell gene therapy for cystinosis, but also our findings on the cellular mechanism of HSPC-mediated tissue preservation led to the application of this strategy to other disorders including the neuro-muscular degenerative disease, Friedreich’s ataxia.

View CV

22nd Annual Meeting
April 29 – May 2 | Washington D.C.