Nicolas Wein, PhD

Nationwide Children's Hospital, Assistant Professor

What is your current professional status?

Assistant Professor

What is your work setting?

Academic Institution

What is your scientific area of research?

RNA and DNA editing; Muscular Dystrophy and neurodegenerative disease

Why do you want to be a mentor?

To share my recent experience about how to find job in academia or in industry and what are the necessary step. I spent a lot of time and effort to understand this transitioning process and I would like to share this recent experience with trainee.

As a mentor, what are you hoping to gain from this experience?

First to help young trainee to promote the next generation but also potential research connections.

How important are the following in the selection of a mentee: (1 – 5 scale, 1 = most important, 5 = least important)

  • Compatibility of Scientific Specialties - 3
  • Geographic Location - 5
  • Professional Status / Success - 2
  • Compatibility of Career Path - 4
  • Communication Style - 1

Provide a biography that describes who you are and what you do in the field of gene and/or cell therapy.

My main interests lie in Human Genetics and Gene Therapy. In particular, my research focuses on the pathophysiology and development of therapies for neuromuscular disorders. As a postdoctoral fellow at OSU/Nationwide Children’s Hospital and as a graduate student at the University of Aix-Marseille with Pr. Nicolas Levy, I developed relevant gene transfer and exon-skipping therapies for two neuromuscular disorders and acquired expertise in genome editing via the novel CRISPR/Cas9 system.

My lab focuses on developing pertinent gene therapy strategies for neuromuscular disorders in particular Duchenne Muscular Dystrophy. My lab will focused on RNA and DNA editing as a therapy for neuromuscular disorders, but it also focuses on a more fundamental questions.

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23rd Annual Meeting

May 12-15 | Boston