Marco Weinberg, PhD

Vertex Pharmaceuticals, Associate Director


What is your current professional status?

Associate Director

What is your work setting (i.e. academic institution, government organization, bio-industry/pharmaceutical company, etc.)?

Biotechnology/Pharmaceutical company

What is your scientific area of research?

Gene editing (eg. CRISPR), RNA therapies

Why do you want to be a mentor?

I have benefited immensely from my experience with good mentors. They have helped me in making good decisions in my scientific career. I have always enjoyed mentoring students and junior colleagues and feel strongly in sharing my experience and expertise with others.

As a mentor, what are you hoping to gain from this experience?

I hope to understand key needs and aspirations of the next generation of scientists and to learn more about their scientific interests and pursuits.

How important are the following in the selection of a mentee: (1 – 5 scale, 1 = most important, 5 = least important)

  • Compatibility of Scientific Specialties: 3
  • Geographic Location: 5
  • Professional Status / Success: 3
  • Compatibility of Career Path: 3
  • Communication Style: 2

Please provide a biography that describes who you are and what you do in the field of gene and/or cell therapy:

At Vertex, I lead a team of scientists involved in developing novel nucleic acid therapies for cystic fibrosis, including gene editing modalities like CRISPR. Prior to joining Vertex, I previously held senior academic positions at The Scripps Research Institute, La Jolla, USA and at the University of the Witwatersrand Medical School, South Africa. My research expertise includes the therapeutic development of non-coding RNAs and my career has spanned the gamut of technologies from hammerhead ribozymes and RNA-based transcriptional modulators, to RNAi and CRISPR/Cas9 applications.

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2019
ASGCT Policy Summit
November 4 – 6 | Washington D.C.
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