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ASGCT
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- Gene-modified stem cells: the next generation therapy for complex bone fractures
- Gene Therapy for Prostate Cancer - A New Therapeutic Hope?
- Magic Bullet Targeting Subcellular Organelle: Mitochondria
- Switching on the Lights in Blind Eyes
- Curing Sick Stem Cells via Gene Therapy
- Safety Improvements for Stem Cell "Taxi Cab"
- A Pox on Your Brain Tumor
- Harnessing Stem Cells for Regenerative Medicine
- Tricking the immune system into tolerating a therapeutic protein
- Restoring Muscle Strength in DMD Mice
- Testing a Painless Treatment for Skin Diseases
- When going viral, the right model makes all the difference
- A need to teach tumor-killing viruses not to suppress the immune system
- One Plus One Equals Three in Gene Therapy for Cancer Study
- Repairing the Heart with Bacteria?
- Treating Bowel Cancer with Gene Therapy: Too Much of a Good Thing
- Gene Vector Integration Profiling in Eye and Brain
- Smart Bombs for Targeted Delivery of Therapeutic Small RNAs
- Buldging at the Seeds Abrogates Off-Targeting of siRNAs
- A Tractable Model of Human Cardiac Development
- Triggering Anti-Tumor Killing with Aptamers
- Systemic Delivery Following Pulmonary Administration of Large-Molecule Nucleic Acid Drugs
- Targeting T Cell-Mediated Immune Response in Malaria Vaccination
- Liver Cells Derived from Stem Cells Will be Used to Test New Drugs
- Duchenne Muscular Dystrophy: on a rational road to the cure?
- A novel processing pathway for microRNA molecules with therapeutic potential
- Dual Function in vivo Delivery of an Inhibitory miRNA and a Corrective Protein Encoding Gene
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- Top Genetic and Cellular Researchers Honored at ASGCT 16th Annual Meeting
- A Media Event on Clinical Developments in Gene and Cell Therapy
- Pioneering Researchers Recognized for Scientific Achievements in Gene and Cell Therapy
- ASGCT ANNUAL MEETING TO HIGHLIGHT LATEST ADVANCES IN GENETIC AND CELLLAR THERAPEUTICS
- Targeted Drug Delivery For Cancer Patients
- American Society of Gene & Cell Therapy Online Journal Now Linked with National Institute of Health
- Gene Therapy and Cell Therapy in the News
- Cell Therapy Fights Leukaemia - Nature News
- Paper Published on Systemic Gene Delivery in Large Species for Targeting Spinal Cord, Brain, and Peripheral Tissues for Pediatric Disorders with Funding from Families of Spinal Muscular Atrophy - Families of SMA
- Dan David Prize: Selected Fields 2012
- Researchers Combine Stem Cell with Artificial Chromosome to Treat Duchenne Muscular Dystrophy in Mice - Genetic Engineering & Biotechnology News (GEN)
- No More 'Bubble Boy': Gene Therapy Gives Kids Normal Lives - msnbc.com
- Immune System, Loaded With Remade T-cells, Vanquishes Cancer - NYTimes.com
- Two Unique Funding Opportunities through the NIH Director's Award Programs - NHLBI
- Summit on Cell Therapy for Cancer
- XIXth Annual ESGCT Congress - Abstract Deadline Extended!
- Summit on Cell Therapy for Cancer: A review of cell therapy as cancer immunotherapy
- Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-escalation study - The Lancet
- Gene-therapy enzymes make unpredicted errors - Nature News
- Rebuilding blood vessels through gene therapy
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- Sangamo Gene Therapy Shows Promise in Reducing HIV - The Baltimore Sun
- Cystic Fibrosis Cure Under Threat From £6m Cash Crisis - The Guardian
- Breakthrough: A Tractable Model of Human Cardiac Development - Nicole M. Kane, PhD
- Breakthrough: Buldging at the Seeds Abrogates Off-Targeting of siRNAs - John J. Rossi, PhD
- Stem Cell Therapy: A Process With a Promise - Xconomy, Seattle
- Experimental Treatments for Macular Degeneration - NY Times
- 'Bubble Boy' Celebrates 10 Years - BBC News
- Breakthrough: Triggering Anti-Tumor Killing with Aptamers - John J. Rossi, PhD
- Gene Therapy & Stem Cells Unite - BBC News
- How Your Tax Dollars Save Lives: Gene Therapy - Discover Magazine
- Gene Therapy Used in a Bid to Save a Man's Sight - BBC News
- Gene Therapy Can Protect Against HIV - Nature
- Haemophilia Gene Therapy Shows Early Success - BBC News
- Gene Therapy Offers Hope for Hemophilia B - ABC News
- NIH Establishes the National Center for Advancing Translational Sciences
- "Target 10" Letter from Current and Past Presidents of ASGCT to Dr. Francis Collins
- French Institute Prepares for Gene Therapy Push - Nature
- Stem Cell Eye Therapy Shows Promise - NPR
- Gene therapy 'gave me sight back'
- Stem Cell Therapy Could Regenerate Damaged Heart Muscle After Heart Attacks - ABC News
- Breakthrough: Dual Function in vivo Delivery of an Inhibitory miRNA and a Corrective Protein Encoding Gene - John J. Rossi, PhD
- Gene therapy aids immune disease, says Great Ormond Street Hospital - BBC News
- Researchers Report Progress in Cancer Immunotherapy - LA Times
- ASGCT Letter to OBA Regarding Role of the RAC
- ASGCT Public Comment to OBA Regarding Role of the RAC
- Gene Therapists Ask to Be Released From the RAC - Science Insider
- Cystic-fibrosis gene-therapy trial rescued - Nature
- Bone-marrow transplant reverses Rett syndrome in mice - Nature
- Treating Muscular Dystrophy with Membrane Resealing
- Breakthrough: Treating Muscular Dystrophy with Membrane Resealing - Dongshend Duan, PhD
- SHAPE Really Matters When it Comes to Short Hairpin RNAs
- Breakthrough: SHAPE Really Matters When it Comes to Short Hairpin RNAs - John J. Rossi, PhD
- FDA Commissioner's Fellowship Program Accepting Applications - Deadline: May 25, 2012
- Novel Parkinson's Treatment Reportedly Reverses Symptoms - CBS News
- Promising Safety Profile: Gene therapy Using AAV-Based Delivery Shuttles
- Grant Opportunity: NCATS Therapeutics Discovery Program
- New Cells for Old Limbs
- Amniotic Fluid + Valproic Acid = New Source of Human Stem Cells
- NIDDK Announces Additional Funding for the PAS Titled: "Stimulating Hematology Investigation: New Endeavors (SHINE) (R01)."
- Launch of Stem Cell Therapy Trial Offers Hope for Patients with Inherited Blood Disorder
- European Agency Backs Approval of a Gene Therapy
- Closing In on a Cure for Vision Loss
- Fighting off viral infections after hematopoietic stem cell transplantation: A single treatment that hits many targets.
- Key element of the clinical scale-up manufacturing process used for Glybera® developed by NHLBI, NIH investigators
- Gene Control, Delivered Directly to the Brain
- A New Way to Patch Up Broken Hearts: Repeated Sphere Formation
- John Rossi is fighting HIV with gene therapy
- Gene Therapy Reverses Hearing Loss in Mice
- Gene Therapy Sniffs out another Success
- NIH Researchers Restore Childrens Immune Systems with Refinements in Gene Therapy
- Exon-skipping drug pulls ahead in muscular dystrophy field
- Gene Transfer and Rare Diseases Workshop
- NHLBI Renews Gene Therapy Resource Program
- Researchers at Children's Hospital Los Angeles Identify a Key Aspect of Lung Epithelial Progenitor Cell Behavior
- NIH Revises the NIH Guidelines for Research Involving Recombinant DNA Molecules
- To Combat Alzheimers Scientists Genetically Reprogram 1 Kind of Brain Cell into Another
- Gene therapies need new development models
- Lamarck and the Missing Lnc
- An Antibody to Prevent Antibodies: Toward a Better and Safer Treatment for Pompe Disease
- Glybera receives final approval by the European Commission
- New gene holds promise for understanding Alzheimer's
- An Alternative Treatment to Lung Transplantation.
- An Old Drug with a New Trick! Glucocorticoids Improve Lentiviral Gene Transfer Into Liver Cells
- Hsp40 Gene Therapy Exerts Therapeutic Effects on Polyglutamine Disease Mice via a Non-Cell Autonomous Mechanism
- NHLBI Workshop Cell Therapy for Lung Diseases
- Use of Genetically Modified Stem Cells in Experimental Gene Therapies
- Promising Caravans of Dreams: Establishing safety of long-term rAAV gene therapy for Canavan’s disease
- Notice of Intent to Publish a Funding Opportunity Announcement (FOA) for The Rare Diseases Clinical Research Consortia (U54)
- New Gene Therapy Extends Lives Of Children With Rare Brain Disorder
- Duke doctor: Stem cell therapy might help heart disease patients
- Recent Gene Therapy Advancements for Neurological Diseases
- Cell Therapy Shows Promise for Acute Type of Leukemia
- Ethical and Policy Issues in Genetic Testing and Screening of Children
- Sensing Gene Therapy
- Dual therapies treat blindness in dogs
- NHLBI & NCATS announce funding for products for rare diseases and pediatric markets
- Leading Gene and Cell Therapy Scientists Flock to Salt Lake City for Convention
- Gene therapy shows new signs of promise
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