ASGCT Awards History

Outstanding New Investigator Award Winners

2013
Aravind Asokan, PhD, University of North Carolina at Chapel Hill
A Sweet Side to AAV Biology

Paloma H. Giangrande, PhD, University of Iowa
Targeted-Image Guided RNA (TIGR) Therapies

Michael A. Laflamme, MD, PhD, University of Washington
Cardiac Repair with Human Pluripotent Stem Cells

Ann M. Leen, PhD, Baylor College of Medicine - CAGT
T cell Therapy for Viruses and Cancer

2012
Nicola Brunetti-Pierri,MD, Telethon Institute of Genetics and Medicine, Napoli, Italy
Helper-Dependent Adenoviral Vectors for Hepatocyte Gene Therapy

Marco A. Passini, PhD, Genzyme, Framingham, MA
Gene and Antisense Therapies for Neurodegenerative Disorders

Theresa M. Reineke, PhD, University of Minnesota
Design and Discovery of Glycopolymer Vehicles for the Delivery of Nucleic Acids

Benjamin R. tenOever, PhD, Mount Sinai School of Medicine
Harnessing the Power of Small RNAs in Vector-Mediated Therapeutics

2011
Hiroyuki Nakai, MD, PhD, University of Pittsburgh School of Medicine, Pittsburgh, PA
In Vivo Viral Genome and Capsid Biology of Recombinant AAV Vectors

Miguel Sena-Esteves, PhD, University of Massachusetts Medical School, Worcester, MA
AAV-Mediated Gene Therapy for Neuro-Metabolic Diseases and Brain Tumors

Qizhen Shi, MD, PhD, Medical College of Wisconsin, Milwaukee, WI
Targeting Factor VIII (FVIII) Expression to Platelets for Gene Therapy of Hemophilia A with Inhibitors

2010
Alessandra Biffi, MD, San Raffaele Telethon Institute for Gene Therapy, Milan, Italy
Rendering Hematopoietic Stem Cell Transplantation Efficacious for the Treatment of Lysosomal Disorders

Kevin V. Morris, PhD, Scripps Research Institute, La Jolla, CA
Utilizing the Endogenous Long Non-Coding RNA Pathway in Human Cells to Transcriptionally Modulate Gene Expression

Bakhos A. Tannous, PhD, Massachusetts General Hospital, Charlestown, MA
Ex-Vivo Monitoring of In Vivo Gene and Cell Therapy

Charles P. Venditti, MD, PhD, National Human Genome Research Institute, Bethesda, MD
Gene Therapy for Methylmalonic Acidemia (MMA)

2009
Renier J. Brentjens, MD, PhD, Memorial Sloan-Kettering Cancer Center, New York, NY
Treatment of B-cell Malignancies with CD19 Targeted T-cells

Barbara Savoldo, MD, PhD, Baylor College of Medicine, Houston, TX
Improving T Cell Based Therapies

Tatiana Segura, PhD, University of California-Los Angeles, Los Angeles, CA
Gene Delivery In Three Dimensions

2008
Karen S. Aboody, MD, City of Hope National Medical Center, Duarte CA
Stem Cell-Mediated Cancer Therapy: A Tumor-Selective Gene Delivery Approach

Maciej S. Lesniak, MD, FACS, The University of Chicago, Chicago, IL
Adenoviral Virotherapy for Malignant Brain Tumors

Dmitry M. Shayakhmetov, PhD, University of Washington, Seattle, WA
Adenovirus-Host Interplay and the Development of Efficient Vectors for Gene Therapy

2007
Gianpietro Dotti, MD, Baylor College of Medicine, Houston, TX
Genetic Modifications of T Cells for Adoptive Immunotherapy in Cancer Patients

Akseli E. Hemminki, MD, PhD, University of Helsinki, Helsinki, Finland
Oncolytic Adenoviruses for Killing of Cancer Initiating Cells

Philip Ng, PhD, Baylor College of Medicine, Houston, TX
Gene Therapy with Helper-Dependant Adenoviral Vectors

Derek Persons, MD, PhD, St. Jude Children’s Research Hospital, Memphis, TN
Progress Toward Safe and Effective Gene Therapy for β-Thalassemia and Sickle Cell Disease

2006
Alberto Auricchio, MD, Telethon Institute of Genetics & Medicine, Napoli, Italy
AAV Serotypes for Gene Therapy of Inherited Human Diseases

Dongsheng Duan, PhD, University of Missouri School of Medicine, Columbia, MO
Pushing the Limit: Making a Small Virus to Work for a Large Gene

Salima Hacein-Bey Abina, PhD, INSERM U 429, Paris, France
Gene Therapy for Severe Combined Immunodeficiency X1

Punam Malik, MD, Children’s Hospital Los Angeles, Los Angeles, CA
Gene Therapy for Red Blood Cell Disorders

2005
Chiara Bonini, MD, Fondazione Centro S. Raffaele Del Monte Tabor, Milan, Italy
Gene Transfer into Peripheral Blood T Lymphocytes: Clinical Benefits and Safety Profile

Michael Kaplitt, MD, PhD, Weill Medical College of Cornell University, New York, NY
Development of Human Gene Therapy for Neurodegenerative Disorders

2004
Michael A. Barry, PhD, Baylor College of Medicine, Houston, TX
Cell-Targeting Technologies for Gene Therapy

Laurence JN Cooper, MD, PhD, City of Hope National Medical Center, Duarte, CA
T-cell Therapy for Malignant B Cells

Matthew Weitzman, PhD, Salk Institute, La Jolla, CA
Lessons from the Battleground of Virus-Host Interactions

2003
Alessandro Aiuti, MD, PhD, Fondazione Centro San Raffaele, Milan, Italy
Gene Therapy for ADA-Deficient SCID

Roland W. Herzog, PhD, Children’s Hospital of Philadelphia, Philadelphia, PA
Immunology of Factor IX Gene Transfer

Christof von Kalle, MD, Cincinnati Children’s Hospital, Cincinnati, OH
Vector Insertion in Gene Modified Human Hematopoiesis

Outstanding Achievement Award Winners

2013
Mark A. Kay, MD, PhD Stanford University School of Medicine
Deciphering Vector and Non-coding RNA Biology: A New Frontier in Nucleic Acid based Therapies.

2012
David A. Williams, MD Children's Hospital Boston, Boston, MA
25 Years in Translation: The Hematopoietic Microenvironment and HSC Gene Therapy

2011
Malcolm K. Brenner, MD, PhD, Baylor College of Medicine, Houston, TX
Cell and Gene Therapy - Putting it Together

2010
Katherine A. High, MD, The Children’s Hospital of Philadelphia, Philadelphia, PA
Gene Therapy for Genetic Disease: Hemophilia as a Paradigm

2009
Inder Verma, PhD, The Salk Institute, La Jolla, CA
25 Years of Gene Therapy: Ups and Downs

2008
R. Jude Samulski, PhD, University of North Carolina at Chapel Hill, Chapel Hill, NC
AAVolution of a Smart Virus