Resources for Patients

Currently there are no FDA approved gene therapy products in the United States. Gene therapy products are still being studied to assess their safety and efficacy in a wide variety of diseases, from cancer, to genetic diseases, to HIV/AIDS. Promising treatments that are not yet licensed are generally only available through a clinical trial.

Answers to frequently asked questions about clinical trials can be found at: About Clinical Trials. Specific information of ongoing gene therapy clinical trials, including potential participation in a research study, can be found at Finding a Clinical Trial. To view a list of patient organizations that maintain websites with helpful information for patients considering gene therapy please see Patient Advocacy Groups that support ASGCT and Sites of Interest for more details.